Lumasiran, an RNAi therapeutic for primary hyperoxaluria type 1
- Sander F. Garrelfs
- , Yaacov Frishberg
- , Sally A. Hulton
- , Michael J. Koren
- , William D. O’Riordan
- , Pierre Cochat
- , Georges Deschênes
- , Hadas Shasha-Lavsky
- , Jeffrey M. Saland
- , William G. van’t Hoff
- , Daniel G. Fuster
- , Daniella Magen
- , Shabbir H. Moochhala
- , Gesa Schalk
- , Eva Simkova
- , Jaap W. Groothoff
- , David J. Sas
- , Kristin A. Meliambro
- , Jiandong Lu
- , Marianne T. Sweetser
- University of Amsterdam
- Shaare Zedek Medical Center
- Birmingham Women's and Children's NHS Foundation Trust
- Jacksonville Ctr Clin Res
- eStudySite
- Université de Lyon
- Hôpital Robert Debré AP-HP
- Western Galilee Medical Center of Nahariya
- Icahn School of Medicine at Mount Sinai
- Great Ormond Street Hospital for Children NHS Foundation Trust
- University of Bern
- Rambam Health Care Campus Israel
- Royal Free London NHS Foundation Trust
- University of Bonn
- Al Jalila Children's Hospital
- Mayo Clinic Rochester, MN
- Alnylam Pharmaceuticals
Research output: Contribution to journal › Article › peer-review
443
Scopus
citations